Table 1

Transgenic Rodent Models


Dr. Goldstein
Dr. Keppler
Dr. Littman

Characteristics of Humanized Rodent Models



Strain
Full-length LTR-regulated HIV provirus and CD-promoter regulated human cyclin T1 expressed as transgenes in mice
Human CD4, CCR5 and cycin T 1 expressed as transgenes in Sprague-Dawley rats
Human CD4, CCR5 and cycin T 1 expressed as transgenes in mice
# mice/donor
NA
NA
NA
Source of human cells
NA
NA
NA
Method of isolation
NA
NA
NA
Pre-transplant treatment-mice
NA
NA
NA
Pre-transplant treatment-cells
NA
NA
NA
Time frame from construction to experimental use
immediately
Immediately
immediately
Location of human hematopoiesis
NA
NA
NA
Location of human Thymopoiesis
NA
NA
NA
Reproducibility of engraftment (% mice engrafted)
NA
NA
NA
Identity of specific human leukocytes present
NA
NA
NA
Populated tissues
HIV provirus and infectious HIV produced by CD4 lymphocytes, macrophages, DC and microglia in all organs analyzed
Human transgenes expressed in rat CD4 lymphocytes, macrophages and microglia in all tissues analyzed
Mouse CD4 T cells and monocyte lineages, including macrophages, dendritic cells, and microglia
Characteristics of HIV Infection of Humanized Rodent Models



HIV-specific immune response
None
Robust seroconversion, cellular responses not analyzed.
not examined
Tropism/clade of infecting HIV
R5- HIV-JR-CSF
R5 HIV-1 (YU-2 and V3 loop recombinant NL4-3) for CD4/CCR5-tg; NL4-3 for CD4/CXCR4-tg (unpublished)
R5 HIV strains (CCR5 Tg mice) and X4 strains (CXCR4 Tg mice)
Target cells infected
All cells
CD4 T-cells, macrophages
CD4+ T cells, macrophages, microglia
Level of plasma HIV viremia
102~105 copies RNA/ml
2 × 102 RNA/ml (transient)
not observed
Duration of the infection
Life of the mouse
Low level viremia up to 7 weeks, low levels of 2-LTR circles at 6 months
not observed
Replication kinetics
Inducible by cellular activation
NA
NA
In vivo generation of ART resistance
NA
NA
NA
Treatment of HIV Infection Using Humanized Rodent Models


Not examined due to lack of replication in vivo
ART to block transmission
NA
Pre-EP and post-EP for efavirenz, enfuvirtide
NA
Microbicide to block transmission
NA
NA
NA
ART to control replication
NA
NA
NA
Emergence of resistance to ART
NA
NA
NA
Elimination of HIV reservoirs
NA
NA
NA
HSC gene therapy to protect progeny cells
NA
NA
NA
CD4 T cell gene therapy to protect cells
NA
NA
NA
Immune-based Therapy of HIV Infection Using Humanized Rodent Models



Preventive HIV vaccines
NA
In progress (humoral immunity)
NA
Treatment HIV vaccines
NA
NA
NA
Adoptive Anti-HIV Ig therapy
NA
NA
NA
Adoptive Anti-HIV CTL therapy
NA
NA
NA
Immunoadjuvent therapy
NA
NA
NA
Investigation of HIV Pathogenesis


Not yet examined due to lack of replication
Contribution of HIV genes to pathogenesis
yes
NA
NA
HIV-mediated CD4-depletion-lymphoid
yes
NA
NA
HIV-mediated CD4-depletion-mucosal
yes
NA
NA
Effects of co-factors on replication
yes
CD4, CCR5, CXCR4, CyclinT1
CD4, CCR5, CXCR4, Cyclin T1, DC-SIGN
Effects of co-infection e.g. mTb on replication
yes
NA
NA
End organ dysfunction
yes
NA
NA

NA = not applicable

Goldstein AIDS Research and Therapy 2008 5:3   doi:10.1186/1742-6405-5-3